Why Sarepta? Why Now?
The promise of genetic medicine has arrived, and Sarepta is at the forefront. We hold a leadership position in Duchenne muscular dystrophy (Duchenne) and are building a robust portfolio of programs across muscle, central nervous system, and cardiac diseases. In 2023, we launched our fourth therapy and the first ever gene therapy to treat Duchenne.
We’re looking for people who see unlimited potential in themselves and who are motivated by an unwavering commitment to patients.
What Sarepta Offers
At Sarepta, we care deeply about all the people in our community and believe in the importance of supporting them in all aspects of their lives. We aspire to maintain a culture that acknowledges people bring their whole selves to work, and we will strive to help everyone in our community integrate their work and personal lives while maintaining productivity.
The Importance of the Role
The Opportunity to Make a Difference
Explore, establish, and maintain 3D liver models or transwell culture systems that more accurately represent physiological liver environments.
Perform AAV transduction experiments under both control and steatosis conditions to evaluate liver injury phenotypes.
Conduct molecular assays—including ddPCR, RT‑ddPCR, and ELISA—to quantify relevant injury or mechanistic markers.
Contribute to assay development and optimization for mechanistic endpoints such as:
Steatosis markers
Fibrosis markers
Oxidative stress indicators
Apoptosis markers
Assist with experimental planning, sample processing, data organization, and preliminary data interpretation.
Summarize experimental findings in a scientific presentation delivered to the team at the end of the internship.
Maintain accurate and detailed electronic lab records in accordance with scientific and organizational standards.
More about You
Currently pursuing a bachelor's degree, master's degree in biology, Molecular Biology, Biochemistry, Biomedical Engineering, Pharmacology, or a related scientific discipline.
Prior laboratory experience in cell culture or molecular biology preferred (coursework or lab rotations acceptable).
Familiarity with assays such as PCR, ELISA, or cell‑based assays is a plus.
Strong attention to detail and commitment to producing high‑quality, reproducible data.
Ability to follow scientific protocols, ask thoughtful questions, and adapt to new experimental techniques.
Strong communication, organization, and collaboration skills.
Interest in therapeutic development, AAV biology, or toxicology research.
Program Timeline
This application is for a 12-week summer internship program that will start on May 18th and conclude on August 7th, 2026.
What Now?
We’re always looking for solution-oriented, critical thinkers.
So, if you’re comfortable with ambiguity and candor, relish challenging yourself, and place kindness and integrity at the forefront of how you approach your peers and work, then we encourage you to apply.
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What We Do
Sarepta Therapeutics, headquartered in Cambridge, Massachusetts, is a global biotechnology company on an urgent mission: engineer precision genetic medicine for rare diseases that devastate lives and cut futures short. We hold leadership positions in Duchenne muscular dystrophy (DMD) and limb-girdle muscular dystrophies (LGMDs), and we currently have more than 40 programs in various stages of development. Our vast pipeline is driven by our multi-platform Precision Genetic Medicine Engine in gene therapy, RNA and gene editing. For information on our Community Guidelines, please visit sarepta.com/community-guidelines. We want to share a reminder with all job seekers and candidates regarding the persistence of recruiting fraud. Please read a message about recruiting fraud and steps you can take to protect yourself here: https://www.sarepta.com/recruiting-fraud
